Real-World Evidence Studies Highlight Cost Burden of Breakthrough Hemolysis Events in Complement Inhibitor-Treated PNH

Paroxysmal Nocturnal Hemoglobinuria (PNH) is a rare, life-threatening blood disorder characterized by the destruction of red blood cells (hemolysis), blood clots, and impaired bone marrow function. This condition is caused by a mutation in the PIGA g...